CAS 2591588-58-6

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Sinónimos:

• [Synonyms]

Rugonersen sodium

CAS: 2591588-58-6

Rugonersen sodium is a locked nucleic acid (LNA)-modified antisense oligonucleotide (ASO) designed to reduce the silencing of ubiquitin protein ligase E3A (UBE3A). Angelman syndrome (AS) refers to a severe neurodevelopmental disorder caused by the loss of neuronal E3 ligase UBE3A, and Rugonersen has been studied for its potential use in the treatment of AS.

Fórmula: C₂₀₄H₂₃₅N₆₃Na₁₉O₁₀₉P₁₉S₁₉

Peso molecular: 6948.00

Ref: TM-T88371