Informazioni sul prodotto
Eteplirsen is a small molecule that inhibits the initiation of mRNA translation by binding to the large ribosomal subunit. It has been shown to improve cardiac function in animal models with Duchenne muscular dystrophy and may be useful for the treatment of other diseases, such as autoimmune diseases. Eteplirsen is used in clinical trials for Duchenne muscular dystrophy, and has shown promising results in terms of efficacy and safety. This drug also has pharmacological properties that are similar to those of ataluren, an agent that was previously tested as a potential treatment for Duchenne muscular dystrophy.
Proprietà chimiche
Richiesta tecnica su: 3D-FE162098 Eteplirsen
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